Cell & Gene Replacement Therapy

[blank_start]Gene therapy[blank_end] aims to treat or cure [blank_start]genetic[blank_end] abnormalities by replacing [blank_start]faulty[blank_end] genes with [blank_start]healthy[blank_end] ones.

Gene therapy is being used for single-gene disorders such as

The Human Genome Project has revealed the location of [blank_start]4000[blank_end] potentially faulty genes

Any disorder resulting in the loss or injury to normal cells is a potential candidate to [blank_start]cell[blank_end] replacement therapy

Which of the following TWO disorders are becoming potential candidates for cell replacement therapy?

Cell replacement therapy for the [blank_start]nervous system[blank_end] involves the replacement of [blank_start]dying[blank_end] neurons with [blank_start]healthy[blank_end] neuronal tissue

In Alzheimer's the cause for a shrunken brain size is due to

[blank_start]Alzheimer's disease[blank_end] impacts the [blank_start]cerebral cortex[blank_end] and areas responsible for language, reasoning and [blank_start]social behavior[blank_end].

What kind of cells are used in cell replacement therapy?

The primary objective of [blank_start]tissue engineering[blank_end] is to restore healthy [blank_start]organs[blank_end] and tissues for patients and thus eliminate the need for tissue/organ transplants or [blank_start]artificial[blank_end] transplants.